26711 Aliso Creek Road # 200B, Aliso Viejo, CA 92656 pcdeficiency@gmail.com (949) 280-1455
Partnership
We are honored to announce our partnership with Dr. Miguel Sena-Esteves for the research and investigation of AAV gene-therapy for Pyruvate Carboxylase Deficiency.
In the initial pre-clinical phase of our project, we will commence by synthesizing AAV vectors and optimizing them. Concurrently, we will initiate the development of animal models as a critical step towards clinical phase.
To read more about his research, please follow the link below:
Partnership
In the initial pre-clinical phase of our project, we will commence by synthesizing AAV vectors and optimizing them. Concurrently, we will initiate the development of animal models as a critical step towards clinical phase.
To read more about his research, please follow the link below:
https://www.umassmed.edu/cancer-center/research/research-faculty-staff/sena-esteves-miguel/